Table of Content
Introduction
Sickle Cell Disease - Overview
Sickle Cell Disease - Therapeutics Development
Sickle Cell Disease - Therapeutics Assessment
Sickle Cell Disease - Companies Involved in Therapeutics Development
Sickle Cell Disease - Drug Profiles
Sickle Cell Disease - Dormant Projects
Sickle Cell Disease - Discontinued Products
Sickle Cell Disease - Product Development Milestones
Appendix
List of Figures
List of Figures
Number of Products under Development for Sickle Cell Disease, 2021
Number of Products under Development by Companies, 2021
Number of Products under Development by Universities/Institutes, 2021
Number of Products by Top 10 Targets, 2021
Number of Products by Stage and Top 10 Targets, 2021
Number of Products by Top 10 Mechanism of Actions, 2021
Number of Products by Stage and Top 10 Mechanism of Actions, 2021
Number of Products by Top 10 Routes of Administration, 2021
Number of Products by Stage and Top 10 Routes of Administration, 2021
Number of Products by Top 10 Molecule Types, 2021
Number of Products by Stage and Top 10 Molecule Types, 2021
List of Tables
List of Tables
Number of Products under Development for Sickle Cell Disease, 2021
Number of Products under Development by Companies, 2021
Number of Products under Development by Universities/Institutes, 2021
Products under Development by Companies, 2021
Products under Development by Universities/Institutes, 2021
Number of Products by Stage and Target, 2021
Number of Products by Stage and Mechanism of Action, 2021
Number of Products by Stage and Mechanism of Action, 2021 (Contd..1)
Number of Products by Stage and Route of Administration, 2021
Number of Products by Stage and Molecule Type, 2021
Sickle Cell Disease - Pipeline by Agios Pharmaceuticals Inc, 2021
Sickle Cell Disease - Pipeline by Alfasigma SpA, 2021
Sickle Cell Disease - Pipeline by Alkermes Plc, 2021
Sickle Cell Disease - Pipeline by Angiocrine Bioscience Inc, 2021
Sickle Cell Disease - Pipeline by Annexin Pharmaceuticals AB, 2021
Sickle Cell Disease - Pipeline by Aruvant Sciences Inc, 2021
Sickle Cell Disease - Pipeline by Aviceda Therapeutics, 2021
Sickle Cell Disease - Pipeline by Axcella Health Inc, 2021
Sickle Cell Disease - Pipeline by Beam Therapeutics Inc, 2021
Sickle Cell Disease - Pipeline by Bellicum Pharmaceuticals Inc, 2021
Sickle Cell Disease - Pipeline by bluebird bio Inc, 2021
Sickle Cell Disease - Pipeline by Bristol Myers Squibb Co, 2021
Sickle Cell Disease - Pipeline by Brooklyn ImmunoTherapeutics Inc, 2021
Sickle Cell Disease - Pipeline by C4X Discovery Holdings Plc, 2021
Sickle Cell Disease - Pipeline by Cannabis Science Inc, 2021
Sickle Cell Disease - Pipeline by Cell Source Inc, 2021
Sickle Cell Disease - Pipeline by Cetya Therapeutics Inc, 2021
Sickle Cell Disease - Pipeline by CRISPR Therapeutics AG, 2021
Sickle Cell Disease - Pipeline by CSL Ltd, 2021
Sickle Cell Disease - Pipeline by Daiichi Sankyo Co Ltd, 2021
Sickle Cell Disease - Pipeline by Editas Medicine Inc, 2021
Sickle Cell Disease - Pipeline by Emmaus Life Sciences Inc, 2021
Sickle Cell Disease - Pipeline by Epidestiny Inc, 2021
Sickle Cell Disease - Pipeline by Epizyme Inc, 2021
Sickle Cell Disease - Pipeline by ExCellThera Inc, 2021
Sickle Cell Disease - Pipeline by Forma Therapeutics Inc, 2021
Sickle Cell Disease - Pipeline by Fulcrum Therapeutics Inc, 2021
Sickle Cell Disease - Dormant Projects, 2021
Sickle Cell Disease - Discontinued Products, 2021