Table of Content


Introduction
Acid Sphingomyelise Deficiency (Niemann-Pick - Overview
Acid Sphingomyelise Deficiency (Niemann-Pick - Therapeutics Development
Acid Sphingomyelise Deficiency (Niemann-Pick - Therapeutics Assessment
Acid Sphingomyelise Deficiency (Niemann-Pick - Companies Involved in Therapeutics Development
Acid Sphingomyelise Deficiency (Niemann-Pick - Drug Profiles
Acid Sphingomyelise Deficiency (Niemann-Pick - Dormant Projects
Acid Sphingomyelise Deficiency (Niemann-Pick - Discontinued Products
Acid Sphingomyelise Deficiency (Niemann-Pick - Product Development Milestones
Appendix



List of Figures

List of Figures
Number of Products under Development for Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C, 2021
Number of Products under Development by Companies, 2021
Number of Products under Development by Universities/Institutes, 2021
Number of Products by Top 10 Targets, 2021
Number of Products by Stage and Top 10 Targets, 2021
Number of Products by Top 10 Mechanism of Actions, 2021
Number of Products by Stage and Top 10 Mechanism of Actions, 2021
Number of Products by Routes of Administration, 2021
Number of Products by Stage and Routes of Administration, 2021
Number of Products by Molecule Types, 2021
Number of Products by Stage and Molecule Types, 2021

List of Tables

List of Tables
Number of Products under Development for Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C, 2021
Number of Products under Development by Companies, 2021
Number of Products under Development by Companies, 2021 (Contd..1)
Number of Products under Development by Universities/Institutes, 2021
Products under Development by Companies, 2021
Products under Development by Companies, 2021 (Contd..1)
Products under Development by Universities/Institutes, 2021
Number of Products by Stage and Target, 2021
Number of Products by Stage and Mechanism of Action, 2021
Number of Products by Stage and Route of Administration, 2021
Number of Products by Stage and Molecule Type, 2021
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by Amicus Therapeutics Inc, 2021
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by Chameleon Biosciences Inc, 2021
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by Cyclo Therapeutics Inc, 2021
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by CycloLab Cyclodextrin Research and Development Laboratory Ltd, 2021
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by E-scape Bio Inc, 2021
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by Endece LLC, 2021
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by Evox Therapeutics Ltd, 2021
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by Gene Therapy Research Institution Co Ltd, 2021
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by IntraBio Ltd, 2021
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by Jewell Laboratories LLC, 2021
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by Mandos LLC, 2021
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by Merck & Co Inc, 2021
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by Okklo Life Sciences BV, 2021
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by Oraxion Therapeutics Inc, 2021
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by Orphazyme A/S, 2021
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by Perlara PBC, 2021
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by Prevacus Inc, 2021
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by Scenic Biotech BV, 2021
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by SOM Biotech SL, 2021
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by StrideBio Inc, 2021
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Dormant Projects, 2021