Table of Content



Introduction
Alpha-1 Antitrypsin Deficiency (A1AD) - Overview
Alpha-1 Antitrypsin Deficiency (A1AD) - Therapeutics Development
Alpha-1 Antitrypsin Deficiency (A1AD) - Therapeutics Assessment
Alpha-1 Antitrypsin Deficiency (A1AD) - Companies Involved in Therapeutics Development
Alpha-1 Antitrypsin Deficiency (A1AD) - Drug Profiles
Alpha-1 Antitrypsin Deficiency (A1AD) - Dormant Projects
Alpha-1 Antitrypsin Deficiency (A1AD) - Discontinued Products
Alpha-1 Antitrypsin Deficiency (A1AD) - Product Development Milestones
Appendix



List of Figures


List of Figures
Number of Products under Development for Alpha-1 Antitrypsin Deficiency (A1AD), 2021
Number of Products under Development by Companies, 2021
Number of Products by Targets, 2021
Number of Products by Stage and Targets, 2021
Number of Products by Mechanism of Actions, 2021
Number of Products by Stage and Mechanism of Actions, 2021
Number of Products by Routes of Administration, 2021
Number of Products by Stage and Routes of Administration, 2021
Number of Products by Molecule Types, 2021
Number of Products by Stage and Molecule Types, 2021

List of Tables


List of Tables
Number of Products under Development for Alpha-1 Antitrypsin Deficiency (A1AD), 2021
Number of Products under Development by Companies, 2021
Number of Products under Development by Companies, 2021 (Contd..1)
Products under Development by Companies, 2021
Products under Development by Companies, 2021 (Contd..1)
Products under Development by Companies, 2021 (Contd..2)
Number of Products by Stage and Target, 2021
Number of Products by Stage and Mechanism of Action, 2021
Number of Products by Stage and Route of Administration, 2021
Number of Products by Stage and Molecule Type, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Alnylam Pharmaceuticals Inc, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Apic Bio Inc, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Applied Genetic Technologies Corp, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Arrowhead Pharmaceuticals Inc, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Beam Therapeutics Inc, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Caravella Biopharma SA, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Centessa Pharmaceuticals Plc, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Dicerna Pharmaceuticals Inc, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Editas Medicine Inc, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Evolve Biologics Inc, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Grifols SA, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Inhibrx Inc, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Intellia Therapeutics Inc, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by International Stem Cell Corp, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Kamada Pharmaceuticals, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Krystal Biotech Inc, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by LEXEO Therapeutics LLC, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Liminal BioSciences Inc, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Logicbio Therapeutics Inc, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Mereo Biopharma Group Plc, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Moderna Inc, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by pH Pharma Co Ltd, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by PlantForm Corp, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Promethera Biosciences SA, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Renovion Inc, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Santhera Pharmaceuticals Holding AG, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Shape Therapeutics Inc, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Takeda Pharmaceutical Co Ltd, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Vera Therapeutics Inc, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Vertex Pharmaceuticals Inc, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Pipeline by Wave Life Sciences Ltd, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Dormant Projects, 2021
Alpha-1 Antitrypsin Deficiency (A1AD) - Dormant Projects, 2021 (Contd..1)
Alpha-1 Antitrypsin Deficiency (A1AD) - Discontinued Products, 2021