Table of Content


Introduction
Pompe Disease - Overview
Pompe Disease - Therapeutics Development
Pompe Disease - Therapeutics Assessment
Pompe Disease - Companies Involved in Therapeutics Development
Pompe Disease - Drug Profiles
Pompe Disease - Dormant Projects
Pompe Disease - Discontinued Products
Pompe Disease - Product Development Milestones
Appendix



List of Figures


Number of Products under Development for Pompe Disease, H2 2020
Number of Products under Development by Companies, H2 2020
Number of Products under Development by Universities/Institutes, H2 2020
Number of Products by Targets, H2 2020
Number of Products by Stage and Targets, H2 2020
Number of Products by Mechanism of Actions, H2 2020
Number of Products by Stage and Mechanism of Actions, H2 2020
Number of Products by Routes of Administration, H2 2020
Number of Products by Stage and Routes of Administration, H2 2020
Number of Products by Molecule Types, H2 2020
Number of Products by Stage and Molecule Types, H2 2020


List of Tables


Number of Products under Development for Pompe Disease, H2 2020
Number of Products under Development by Companies, H2 2020
Number of Products under Development by Companies, H2 2020 (Contd..1), H2 2020
Number of Products under Development by Universities/Institutes, H2 2020
Products under Development by Companies, H2 2020
Products under Development by Companies, H2 2020 (Contd..1), H2 2020
Products under Development by Universities/Institutes, H2 2020
Number of Products by Stage and Target, H2 2020
Number of Products by Stage and Mechanism of Action, H2 2020
Number of Products by Stage and Route of Administration, H2 2020
Number of Products by Stage and Molecule Type, H2 2020
Pompe Disease - Pipeline by Abeona Therapeutics Inc, H2 2020
Pompe Disease - Pipeline by Amicus Therapeutics Inc, H2 2020
Pompe Disease - Pipeline by Asklepios BioPharmaceutical Inc, H2 2020
Pompe Disease - Pipeline by Audentes Therapeutics Inc, H2 2020
Pompe Disease - Pipeline by Avidity Biosciences Inc, H2 2020
Pompe Disease - Pipeline by AVROBIO Inc, H2 2020
Pompe Disease - Pipeline by eleva GmbH, H2 2020
Pompe Disease - Pipeline by EpiVax Inc, H2 2020
Pompe Disease - Pipeline by Etubics Corp, H2 2020
Pompe Disease - Pipeline by Genzyme Corp, H2 2020
Pompe Disease - Pipeline by Icagen Inc, H2 2020
Pompe Disease - Pipeline by JCR Pharmaceuticals Co Ltd, H2 2020
Pompe Disease - Pipeline by M6P Therapeutics, H2 2020
Pompe Disease - Pipeline by NanoMedSyn SAS, H2 2020
Pompe Disease - Pipeline by Oxyrane Belgium NV, H2 2020
Pompe Disease - Pipeline by Pharming Group NV, H2 2020
Pompe Disease - Pipeline by RespireRx Pharmaceuticals Inc, H2 2020
Pompe Disease - Pipeline by Sarepta Therapeutics Inc, H2 2020
Pompe Disease - Pipeline by Spark Therapeutics Inc, H2 2020
Pompe Disease - Pipeline by Takeda Pharmaceutical Co Ltd, H2 2020
Pompe Disease - Dormant Projects, H2 2020
Pompe Disease - Discontinued Products, H2 2020