Table of Content



Introduction
Acid Sphingomyelise Deficiency Type C - Overview
Acid Sphingomyelise Deficiency Type C - Therapeutics Development
Acid Sphingomyelise Deficiency Type C - Therapeutics Assessment
Acid Sphingomyelise Deficiency Type C - Companies Involved in Therapeutics Development
Acid Sphingomyelise Deficiency Type C - Drug Profiles
Acid Sphingomyelise Deficiency Type C - Dormant Projects
Acid Sphingomyelise Deficiency Type C - Discontinued Products
Acid Sphingomyelise Deficiency Type C - Product Development Milestones
Appendix



List of Figures



Number of Products under Development for Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C, H2 2020
Number of Products under Development by Companies, H2 2020
Number of Products under Development by Universities/Institutes, H2 2020
Number of Products by Top 10 Targets, H2 2020
Number of Products by Stage and Top 10 Targets, H2 2020
Number of Products by Top 10 Mechanism of Actions, H2 2020
Number of Products by Stage and Top 10 Mechanism of Actions, H2 2020
Number of Products by Routes of Administration, H2 2020
Number of Products by Stage and Routes of Administration, H2 2020
Number of Products by Molecule Types, H2 2020
Number of Products by Stage and Molecule Types, H2 2020


List of Tables



Number of Products under Development for Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C, H2 2020
Number of Products under Development by Companies, H2 2020
Number of Products under Development by Universities/Institutes, H2 2020
Products under Development by Companies, H2 2020
Products under Development by Universities/Institutes, H2 2020
Number of Products by Stage and Target, H2 2020
Number of Products by Stage and Mechanism of Action, H2 2020
Number of Products by Stage and Route of Administration, H2 2020
Number of Products by Stage and Molecule Type, H2 2020
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by Amicus Therapeutics Inc, H2 2020
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by Cyclo Therapeutics Inc, H2 2020
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by CycloLab Cyclodextrin Research and Development Laboratory Ltd, H2 2020
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by E-scape Bio Inc, H2 2020
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by Endece LLC, H2 2020
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by Evox Therapeutics Ltd, H2 2020
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by Gene Therapy Research Institution Co Ltd, H2 2020
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by IntraBio Ltd, H2 2020
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Pipeline by Jewell Laboratories LLC, H2 2020
Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Type C - Dormant Projects, H2 2020