Table of Content

1 INTRODUCTION
1.1 Study Assumptions
1.2 Scope of the Study


2 RESEARCH METHODOLOGY


3 EXECUTIVE SUMMARY


4 MARKET DYNAMICS
4.1 Market Overview
4.2 Market Drivers
4.2.1 Launch of Novel Drugs
4.2.2 Continued Uptake of Long Term Therapies
4.3 Market Restraints
4.3.1 High Treatment Cost
4.4 Porter’s Five Force Analysis
4.4.1 Threat of New Entrants
4.4.2 Bargaining Power of Buyers/Consumers
4.4.3 Bargaining Power of Suppliers
4.4.4 Threat of Substitute Products
4.4.5 Intensity of Competitive Rivalry


5 MARKET SEGMENTATION
5.1 By Route of Administration
5.1.1 Oral
5.1.2 Parenteral
5.2 By Treatment Type
5.2.1 Substrate Reduction Therapy (SRT)
5.2.2 Enzyme Replacement Therapy?(ERT)
5.2.3 Chaperone-Advanced Replacement Therapy (CART)
5.2.4 Supportive Care
5.3 By End User
5.3.1 Hospitals
5.3.2 Diagnostic Centers
5.3.3 Ambulatory Surgical Centers
5.3.4 Others
5.4 Geography
5.4.1 North America
5.4.1.1 United States
5.4.1.2 Canada
5.4.1.3 Mexico
5.4.2 Europe
5.4.2.1 Germany
5.4.2.2 United Kingdom
5.4.2.3 France
5.4.2.4 Italy
5.4.2.5 Spain
5.4.2.6 Rest of Europe
5.4.3 Asia-Pacific
5.4.3.1 China
5.4.3.2 Japan
5.4.3.3 India
5.4.3.4 Australia
5.4.3.5 South Korea
5.4.3.6 Rest of Asia-Pacific
5.4.4 Middle-East and Africa
5.4.4.1 GCC
5.4.4.2 South Africa
5.4.4.3 Rest of Middle-East and Africa
5.4.5 South America
5.4.5.1 Brazil
5.4.5.2 Argentina
5.4.5.3 Rest of South America


6 COMPETITIVE LANDSCAPE
6.1 Company Profiles
6.1.1 Genzyme Corporation
6.1.2 Amicus Therapeutics
6.1.3 Valerion Therapeutics
6.1.4 Audentes Therapeutics
6.1.5 EpiVax, Inc
6.1.6 Oxyrane
6.1.7 Sangamo Therapeutics


7 MARKET OPPORTUNITIES AND FUTURE TRENDS