List of Companies Profiled in the Report
American Gene Technologies
Applied Genetic
Astellas Pharma Inc.
Bayer
Benitec BioPharma
Biogen
Bluebird Bio
Bristol Myers Squibb
Calimmune, Inc. (CSL Behiring)
Cellectis
GeneQuine Biotherapeutics
GenSight Biologics
Gilead Lifesciences, Inc.
Novartis AG
Ocugen, Inc.
Orchard Therapeutics
Oxford Biomedica
Pfizer, Inc.
REGENXBIO Inc.
Sangamo Therapeutics, Inc.
Sanofi
Sarepta Therapeutics, Inc.
Spark Therapeutics (Subsidiary of Roche)
Takeda Pharmaceuticals
Taysha GTx
Transgene
UniQure N. V.
ViGeneron
Voyager Therapeutics
List of Other Companies Mentioned in the Report
2seventy bio, Inc.
AmerisourceBergen
ABL Europe SAS
Ascend Advanced Therapies
Asklepios BioPharmaceutical, Inc.
Atamyo Therapeutics
Aurealis Therapeutics
Autolus Therapeutics plc
BlueRock Therapeutics LP
Cabaletta Bio, Inc.
CANbridge Pharmaceuticals Inc.
Cellares
Coave Therapeutics
Cytonus Therapeutics
Decibel Therapeutics, Inc.
Encellin
Encoded Therapeutics
Exothera S.A.
FUJIFILM Diosynth Biotechnologies
Gadeta B.V.
Genprex, Inc.
Hercules Capital, Inc.
Inhibrx, Inc.
INVO Bioscience
Immatics N.V.
Kadans Science Partner
Karuna Therapeutics, Inc.
Kriya Therapeutics, Inc.
Lexeo Therapeutics, Inc.
Liminal BioSciences, Inc.
MeiraGTx Holdings plc
Miltenyi Biotec
MorphoSys AG
Mytos
NAYA Biosciences
Neurocrine Biosciences, Inc.
Nvelop Therapeutics
Pacira BioSciences, Inc.
PTC Therapeutics, Inc.
Reata Pharmaceuticals, Inc.
Selecta Biosciences
Shinobi Therapeutics
Sio Gene Therapies
Syncona
Taysha Gene Therapies, Inc.
Tome Biosciences
T-Therapeutics
ViaNautis Bio
VectorBuilder
VectorY Therapeutics
Verve Therapeutics, Inc.
Vivet Therapeutics
Xbiome
Xcell Biosciences, Inc.
List of Associations Mentioned in the Report
China’s National Medical Products Administration (NMPA)
Committee for Medicinal Products for Human Use (CHMP)
European Commission (EC)
European Medicines Agency (EMA)
Gene Therapy Net
Informa UK Limited
Journal of General Virology
Ministry of Health, Labour and Welfare (MHLW)
National Center for Biotechnology Information
The Alliance for Regenerative Medicine
The Royal Society
US Food and Drug Administration (FDA)
American Gene Technologies
Applied Genetic
Astellas Pharma Inc.
Bayer
Benitec BioPharma
Biogen
Bluebird Bio
Bristol Myers Squibb
Calimmune, Inc. (CSL Behiring)
Cellectis
GeneQuine Biotherapeutics
GenSight Biologics
Gilead Lifesciences, Inc.
Novartis AG
Ocugen, Inc.
Orchard Therapeutics
Oxford Biomedica
Pfizer, Inc.
REGENXBIO Inc.
Sangamo Therapeutics, Inc.
Sanofi
Sarepta Therapeutics, Inc.
Spark Therapeutics (Subsidiary of Roche)
Takeda Pharmaceuticals
Taysha GTx
Transgene
UniQure N. V.
ViGeneron
Voyager Therapeutics
List of Other Companies Mentioned in the Report
2seventy bio, Inc.
AmerisourceBergen
ABL Europe SAS
Ascend Advanced Therapies
Asklepios BioPharmaceutical, Inc.
Atamyo Therapeutics
Aurealis Therapeutics
Autolus Therapeutics plc
BlueRock Therapeutics LP
Cabaletta Bio, Inc.
CANbridge Pharmaceuticals Inc.
Cellares
Coave Therapeutics
Cytonus Therapeutics
Decibel Therapeutics, Inc.
Encellin
Encoded Therapeutics
Exothera S.A.
FUJIFILM Diosynth Biotechnologies
Gadeta B.V.
Genprex, Inc.
Hercules Capital, Inc.
Inhibrx, Inc.
INVO Bioscience
Immatics N.V.
Kadans Science Partner
Karuna Therapeutics, Inc.
Kriya Therapeutics, Inc.
Lexeo Therapeutics, Inc.
Liminal BioSciences, Inc.
MeiraGTx Holdings plc
Miltenyi Biotec
MorphoSys AG
Mytos
NAYA Biosciences
Neurocrine Biosciences, Inc.
Nvelop Therapeutics
Pacira BioSciences, Inc.
PTC Therapeutics, Inc.
Reata Pharmaceuticals, Inc.
Selecta Biosciences
Shinobi Therapeutics
Sio Gene Therapies
Syncona
Taysha Gene Therapies, Inc.
Tome Biosciences
T-Therapeutics
ViaNautis Bio
VectorBuilder
VectorY Therapeutics
Verve Therapeutics, Inc.
Vivet Therapeutics
Xbiome
Xcell Biosciences, Inc.
List of Associations Mentioned in the Report
China’s National Medical Products Administration (NMPA)
Committee for Medicinal Products for Human Use (CHMP)
European Commission (EC)
European Medicines Agency (EMA)
Gene Therapy Net
Informa UK Limited
Journal of General Virology
Ministry of Health, Labour and Welfare (MHLW)
National Center for Biotechnology Information
The Alliance for Regenerative Medicine
The Royal Society
US Food and Drug Administration (FDA)