1. Alnylam Pharmaceuticals Inc.
2. Alterity Therapeutics Limited
3. Annexon Biosciences
4. AOP Orphan Pharmaceuticals GmbH
5. Bausch Health Companies Inc.
6. Dr. Reddy’s Laboratories Ltd.
7. Hikma Pharmaceuticals PLC
8. Ionis Pharmaceuticals Inc.
9. Ipsen S.A.
10. Lupin Limited
11. Medesis Pharma SA
12. Mitochon Pharmaceuticals Inc.
13. NeuExcell Therapeutics Inc
14. Neurocrine Biosciences Inc.
15. Novartis AG
16. Pfizer Inc.
17. Prilenia Therapeutics B.V.
18. PTC Therapeutics Inc.
19. SOM Innovation Biotech S.A.
20. Sun Pharmaceutical Industries Limited
21. Teva Pharmaceutical Industries Ltd.
22. uniQure N.V.
23. Vaccinex Inc.
24. Vertex Pharmaceuticals Incorporated