1. Genzyme Corp
2. Amicus Therapeutics Inc
3. Valerion Therapeutics LLC
4. Audentes Therapeutics Inc
5. Actus Therapeutics Inc
6. BioMarin Pharmaceutical Inc
7. EpiVax inc
8. Oxyrane Co Ltd.
9. Sangamo BioSciences Inc
10. Avrobio Inc
11. Spark Therapeutics Inc