List of Companies Profiled in the Report
AbbVie Inc.
AstraZeneca
Biogen
Bristol-Myers Squibb Company
F. Hoffmann-La Roche Ltd.
GSK plc
Johnson & Johnson Services, Inc.
Merck & Co., Inc.
Novartis AG
Pfizer Inc.
Sanofi
Vertex Pharmaceuticals Incorporated

List of Other Companies Mentioned in the Report
2seventy bio, Inc.
Alexion
Amgen Inc.
Beam Therapeutics
CRISPR Therapeutics
DJS Antibodies
Incyte
Lilly
Neogene Therapeutics Inc.
Pharmacyclics

List of Associations Mentioned in the Report
European Medicines Agency (EMA)
Indian Council of Medical Research (ICMR)
Italian Medicines Agency (AIFA)
Ministry of Food and Drug Safety (MFDS)
National Organization for Rare Disorders (NORD)
The Canadian Agency for Drugs and Technologies in Health (CADTH)
Spain's National Health System (Sistema Nacional de Salud; SNS)
National Institute of Drug and Food Surveillance (INVIMA)
U.S. Food and Drug Administration (FDA)