• Idorsia Pharmaceuticals
• Protalix
• Sanofi Genzyme
• Sangamo Therapeutics
• 4D Molecular Therapeutics
• Resverlogix Corp
• AVROBIO
• Freeline Therapeutics
• Ozmosis Research Inc.
• CellGenTech Inc.
• uniQure
• Codexis
• Canbridge
• Eleva GmbH
• MP6 therapeutics
• Amicus therapeutics
• Sigilon Therapeutics