AavantiBio Inc
Amicus Therapeutics Inc
Asklepios BioPharmaceutical Inc
Astellas Gene Therapies
Avidity Biosciences Inc
AVROBIO Inc
CANbridge Life Sciences Ltd
Denali Therapeutics Inc
eleva GmbH
EpiVax Inc
Etubics Corp
Genzyme Corp
Icagen Inc
JCR Pharmaceuticals Co Ltd
M6P Therapeutics
Maze Therapeutics Inc
NanoMedSyn SAS
Oxyrane Belgium NV
Pharming Group NV
Provention Bio Inc
RespireRx Pharmaceuticals Inc
Sarepta Therapeutics Inc
Spark Therapeutics Inc
Takeda Pharmaceutical Co Ltd