AavantiBio Inc
Adverum Biotechnologies Inc
Anima Biotech Inc
Biointaxis SL
Cellivery Therapeutics Inc
CRISPR Therapeutics AG
Design Therapeutics Inc
Fratagene Therapeutics Srl
Fulcrum Therapeutics Inc
Jupiter Orphan Therapeutics Inc
Lacerta Therapeutics Inc
Larimar Therapeutics Inc
Novartis Gene Therapies
PTC Therapeutics Inc
Voyager Therapeutics Inc