AavantiBio Inc
Adverum Biotechnologies Inc
Amylyx Pharmaceutical Corp
Anima Biotech Inc
Biointaxis SL
BioMarin Pharmaceutical Inc
Biovista Inc
CRISPR Therapeutics AG
Design Therapeutics Inc
Epirium Bio Inc
Exicure Inc
Fratagene Therapeutics Srl
Fulcrum Therapeutics Inc
Ixchel Pharma LLC
Jupiter Orphan Therapeutics Inc
Lacerta Therapeutics Inc
Larimar Therapeutics Inc
Metro International Biotech LLC
Minoryx Therapeutics sl
Novartis Gene Therapies
PTC Therapeutics Inc
Reata Pharmaceuticals Inc
Retrotope Inc
Seelos Therapeutics Inc.
STATegics Inc
Stealth BioTherapeutics Corp
StrideBio Inc
Voyager Therapeutics Inc