Novartis
Spark Therapeutics
BioGen
Sarepta Therapeutics
Kite Pharma
Amgen
Solid Biosciences Inc.
uniQure NV
MeiraGTX Holdings
Audentis Therapeutics
Regenxbio Inc.
Alnylam Pharmaceuticals
Arrowhead
SQZ Biotechnologies
Bluerock Therapeutics
Zydus Takeda
Intrexon Corporation
Celgene
Roche
Oxford Biomedica
Genethon
Sangamo Biosciences
Juno Therapeutics
Cellectis
Autolus Therapeutics plc
icell Gene Therapeutics
Allogene Therapeutics