Table of Content



List of Tables
List of Figures
Introduction
Global Markets Direct Report Coverage
Inclusion Body Myositis (IBM) - Overview
Inclusion Body Myositis (IBM) - Therapeutics Development
Pipeline Overview
Pipeline by Companies
Products under Development by Companies
Inclusion Body Myositis (IBM) - Therapeutics Assessment
Assessment by Target
Assessment by Mechanism of Action
Assessment by Route of Administration
Assessment by Molecule Type
Inclusion Body Myositis (IBM) - Companies Involved in Therapeutics Development
AAVogen Inc
Abcuro Inc
Alzheon Inc
Cleave Therapeutics Inc
Kv1.3 Therapeutics
Leadiant Biosciences Inc
Milo Biotechnology LLC
Nobelpharma Co Ltd
Orphazyme A/S
PhaseBio Pharmaceuticals Inc
Ultragenyx Pharmaceutical Inc
Inclusion Body Myositis (IBM) - Drug Profiles
ABC-08 - Drug Profile
Product Description
Mechanism Of Action
R&D Progress
aceneuramic acid ER - Drug Profile
Product Description
Mechanism Of Action
R&D Progress
ALZ-507 - Drug Profile
Product Description
Mechanism Of Action
R&D Progress
arimoclomol citrate - Drug Profile
Product Description
Mechanism Of Action
R&D Progress
AVGN-7 - Drug Profile
Product Description
Mechanism Of Action
R&D Progress
dalazatide - Drug Profile
Product Description
Mechanism Of Action
R&D Progress
DEXM-74 - Drug Profile
Product Description
Mechanism Of Action
R&D Progress
Gene therapy To Activate Follistatin For Duchenne Muscular Dystrophy, Becker Muscular Dystrophy And Inclusion Body Myositis - Drug Profile
Product Description
Mechanism Of Action
R&D Progress
PB-1023 - Drug Profile
Product Description
Mechanism Of Action
R&D Progress
Small Molecule to Inhibit VCP/p97 for Neurodegenerative Diseases - Drug Profile
Product Description
Mechanism Of Action
R&D Progress
UX-001P - Drug Profile
Product Description
Mechanism Of Action
R&D Progress
Inclusion Body Myositis (IBM) - Dormant Projects
Inclusion Body Myositis (IBM) - Discontinued Products
Inclusion Body Myositis (IBM) - Product Development Milestones
Featured News & Press Releases
Feb 11, 2020: CytRx highlights recently published data of its licensee Orphazyme A/S Phase 2 trial of Arimoclomol in the treatment of Sporadic Inclusion Body Myositis (sIBM)
Dec 18, 2019: Orphazyme’s arimoclomol receives US fast track desigtion in sporadic inclusion body myositis
May 02, 2019: CytRx Highlights Arimoclomol Clinical Milestone Guidance Provided by Licensee Orphazyme
Apr 29, 2019: CytRx highlights enrollment completion in phase 2/3 clinical trial of Sporadic Inclusion Body Myositis conducted by Arimoclomol Licensee Orphazyme
Apr 23, 2019: Orphazyme’s Phase II/III trial in sporadic Inclusion Body Myositis fully enrolled
Apr 25, 2018: New Data Supports Dalazatide from Kv 1.3 Therapeutics as a Potential Therapy for Inclusion Body Myositis
Dec 14, 2017: Orphazyme Assumes Sponsorship of Phase II/III sIBM Trial
Nov 07, 2017: Orphazyme Receives Orphan Drug Desigtion To Arimoclomol For Inclusion Body Myositis From The U.S. FDA
Aug 22, 2017: Ultragenyx Announces Top-Line Results from Phase 3 Study of Ace-ER in GNE Myopathy
Nov 11, 2016: Ultragenyx Announces Withdrawal of Marketing Authorization Application for Aceneuramic Acid Prolonged Release (Ace-ER) in the European Union
Jul 27, 2016: Ultragenyx Announces Completion of Enrollment in Phase 3 Study of Aceneuramic Acid Extended Release (Ace-ER) in GNE Myopathy
Mar 24, 2016: Arimoclomol shows promise in protein misfolding disease
Mar 23, 2016: New drug shows promise against muscle wasting disease
Oct 02, 2015: Ultragenyx Announces Aceneuramic Acid Prolonged Release Marketing Authorization Application Filed and Accepted for Review by European Medicines Agency
May 28, 2015: Ultragenyx Announces First Patient Enrolled in Global Phase 3 Study of Aceneuramic Acid (Sialic Acid) Extended Release in GNE Myopathy
Appendix
Methodology
Coverage
Secondary Research
Primary Research
Expert Panel Validation
Contact Us
Disclaimer



List of Figures



Number of Products under Development for Inclusion Body Myositis (IBM), H2 2020
Number of Products under Development by Companies, H2 2020
Number of Products by Targets, H2 2020
Number of Products by Stage and Targets, H2 2020
Number of Products by Mechanism of Actions, H2 2020
Number of Products by Stage and Mechanism of Actions, H2 2020
Number of Products by Routes of Administration, H2 2020
Number of Products by Stage and Routes of Administration, H2 2020
Number of Products by Molecule Types, H2 2020
Number of Products by Stage and Molecule Types, H2 2020


List of Tables



Number of Products under Development for Inclusion Body Myositis (IBM), H2 2020
Number of Products under Development by Companies, H2 2020
Products under Development by Companies, H2 2020
Number of Products by Stage and Target, H2 2020
Number of Products by Stage and Mechanism of Action, H2 2020
Number of Products by Stage and Route of Administration, H2 2020
Number of Products by Stage and Molecule Type, H2 2020
Inclusion Body Myositis (IBM) - Pipeline by AAVogen Inc, H2 2020
Inclusion Body Myositis (IBM) - Pipeline by Abcuro Inc, H2 2020
Inclusion Body Myositis (IBM) - Pipeline by Alzheon Inc, H2 2020
Inclusion Body Myositis (IBM) - Pipeline by Cleave Therapeutics Inc, H2 2020
Inclusion Body Myositis (IBM) - Pipeline by Kv1.3 Therapeutics, H2 2020
Inclusion Body Myositis (IBM) - Pipeline by Leadiant Biosciences Inc, H2 2020
Inclusion Body Myositis (IBM) - Pipeline by Milo Biotechnology LLC, H2 2020
Inclusion Body Myositis (IBM) - Pipeline by Nobelpharma Co Ltd, H2 2020
Inclusion Body Myositis (IBM) - Pipeline by Orphazyme A/S, H2 2020
Inclusion Body Myositis (IBM) - Pipeline by PhaseBio Pharmaceuticals Inc, H2 2020
Inclusion Body Myositis (IBM) - Pipeline by Ultragenyx Pharmaceutical Inc, H2 2020
Inclusion Body Myositis (IBM) - Dormant Projects, H2 2020
Inclusion Body Myositis (IBM) - Discontinued Products, H2 2020